Terapia Gênica:
Futuro tratamento para a Esclerose Lateral Amiotrófica?
DOI:
https://doi.org/10.34024/rnc.2006.v14.8778Palavras-chave:
SuplementoResumo
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Métricas
Referências
Nance BN, Ventura AM. Terapia Gênica. Mir L (org.) Genômica. São Paulo: Atheneu, 2004, cap.30.
Federici T, Boulis NM. Gene-based treatment of motor neuron diseases. Muscle Nerve. 2006;33(3):302-323.
Ralph GS, Radcliffe PA, Day DM, Carthy JM, Leroux MA, Lee DC, et al. Silencing mutant SOD1 using RNAi protects against neurodegeneration and extends survival in an ALS model. Nat Med. 2005;11(4):429-433.
Xia XG, Zhou H, Zhou S, Yu Y, Wu R, Xu Z. An RNAi strategy for treatment of amyotrophic lateral sclerosis caused by mutant Cu, Zn superoxide dismutase. J Neurochem. 2005;92(2):362-367.
Azzouz M, Ralph GS, Storkebaum E, Walmsley LE, Mitrophanous KA, Kingsman SM, et al. VEGF delivery with retrogradely transported lentivector prolongs survival in a mouse ALS model. Nature. 2004;429(6990):413-417.
